spinraza

Terminally Ill Children May Be Saved by New Treatment

Most of us take our own lives – and even the lives of our healthy children – for granted. But for an unfortunate minority, rare genetic diseases don’t just threaten to steal lives away; they are serious enough to follow through with it. This is the case with one such genetic disease known as spinal muscular atrophy (SMA), but a recently-released drug holds promise as its first known treatment.